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Development of gene editing strategies for human beta-globin (HBB) gene mutations
Kalkan, Batuhan Mert; Kala, Ezgi Yagmur; Yuce, Melek; Alpaslan, Medine Karadag; Kocabas, Fatih (Elsevier, 2020)Recent developments in gene editing technology have enabled scientists to modify DNA sequence by using engineered endonucleases. These gene editing tools are promising candidates for clinical applications, especially for ...